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SDS & Science Snapshots (2022-07-10)
In this issue: CRISPR-Cas9 turns 10; The promise of Gene Therapy for Rare Disease and Shwachman-Diamond Syndrome (SDS) Welcome to our...
SDS & Science Snapshots (2022-07-03)
In this issue: IRDiRC Working Group Recommendations for rare disease patients; The Access to Rare Indications Act could be a game changer...
SDS & Science Snapshots (2022-06-25)
In this issue: Rare-X report provides update on the true number of rare diseases; new review article on bone marrow failure disorders by...
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